Gael Jesus Pino Alva, 2, was the first patient treated with the new gene therapy developed at St. Jude Children’s Research Hospital and UCSF Benioff Children’s Hospital in San Francisco. Jude Children’s Research Hospital)Ten newborns with the rare genetic disorder known as bubble boy disease were cured with gene therapy, researchers revealed Wednesday. “For immunologists following this disease, gene therapy has always been out there as the hope of the future. Those corrected cells were then reinfused back into the patient, where they proliferated and created healthy immune cells. Brian Sorrentino holds Gael Jesus Pino Alva, who was the first patient treated with the new gene therapy for SCID.

Source: Washington Post April 17, 2019 21:00 UTC