The parents of a baby with a fatal condition have succeeded in their campaign for their son to be treated with the world’s most expensive drug. I didn’t think he had a future.”The drug contains a copy of the missing gene SMN1, allowing it to halt the condition’s progression. After “countless sleepless” night she felt hugely relieved to get the news that the NHS would treat Edward by the middle of August. As the drug is far more effective when administered at a young age, “time is massively of the essence”, Willis said. It’s incredible.”Edward, who was diagnosed at two months, is currently being treated with Spinraza, which is administered by injection every four months.

Source: The Guardian July 11, 2021 06:00 UTC