The technique is an adapted version of the powerful gene editing tool called Crispr. Show Hide Crispr, or to give it its full name, Crispr-Cas9, allows scientists to precisely target and edit pieces of the genome. Crispr is a guide molecule made of RNA, that allows a specific site of interest on the DNA double helix to be targeted. “That is something that is going to stay with us with Crispr or any other tool we develop that cuts DNA. The illness is caused by a mutation in the gene that produces dystrophin, a protein found in muscle fibres.

Source: The Guardian December 07, 2017 17:00 UTC